A focused pipeline.
MGAM advances one rare-disease program, in classic Pelizaeus-Merzbacher disease.
Life Sciences — Active pipeline
Rare-disease programs centered on defined patient populations, focused development strategies, and substantial unmet need.
| Program | Indication | Candidate | Regulatory milestone |
|---|---|---|---|
| MGAM-003Classic PMD | Classic Pelizaeus-Merzbacher diseaseRare pediatric disease | Clemastine fumarate | Rare Pediatric Disease Designation granted |